Hide-and-seek can lead to higher drug prices In Switzerland and other European countries, drug prices are regulated to ensure affordable access to drugs. In the last few years, many European countries have introduced rebate schemes for drugs. In most cases, however, the rebates negotiated with the manufacturer are confidential. This…..
Rentschler Biopharma to build new cell and gene therapy capabilities in the UK Leading German CDMO for biopharmaceuticals, Rentschler Biopharma will establish their manufacturing capability in ATMPs, including Adeno-Assiociated Virus (AAV) vectors for clinical trial supply at the Cell and Gene Therapy (CGT) Catapult facility site in Stevenage. Under the…..
Using precision medicine to uncover and treat new skeletal disorders Researchers of the “Cell Biology and Physiology-LABRET” group of the University of Malaga (UMA), together with the Networking Biomedical Research Center in Bioengineering, Biomaterials and Nanomedicine (CIBER-BBN), have described a new genetic skeletal disorder based on a precision medicine strategy.…..
Vector-Based Gene Therapy and Gene-Editing Products Ongoing Clinical Trials Gene therapies are now a reality. They open new perspectives for the treatment and management of a wide range of rare and common diseases. We have listed ongoing clinical trials using viral vector and gene editing products to get a more…..
A new gene therapy could pave the way to the treatment of mitochondrial dysfunctions Scientists from Trinity College Dublin have developed a new gene therapy approach that offers promise for one day treating dominant optic atrophy (DOA). This eye disease is characterized by degeneration of the optic nerves and primarily…..
AlgoTherapeutix raises €12M to fight against chemotherapy-induced peripheral neuropathy France-based biotechnology company AlgoTherapeutix has raised €12M in a Series A round led by Bpifrance through its InnoBio 2 fund with co-investor Omnes. The proceeds will be used to fund the clinical development of its lead candidate ATX01 up to clinical…..
Record financing for the regenerative medicine sector through Q3 2020 The regenerative medicine sector attracted $15.9 billion in financing through just the first three quarters of the year, shattering the previous record of $13.5 billion Global financing for the regenerative medicine and advanced therapy sector set an annual record of…..
Ultragenyx will build a new gene therapy manufacturing facility in Bedford Ultragenyx Pharmaceutical, a US biopharmaceutical company focused on the identification, acquisition, development, and commercialization of novel products for the treatment of rare and ultra-rare genetic diseases, plans to build a new large-scale gene therapy manufacturing facility in Bedford, Massachusetts.…..
Le site Sanofi Genzyme de Lyon Gerland devient la première plateforme mondiale Sanofi pour la thérapie génique
Le site Sanofi Genzyme de Lyon Gerland devient la première plateforme mondiale Sanofi pour la thérapie génique Quelques jours après le rachat de la biotech néerlandaise Kiadis Pharma et de sa plateforme d'immunothérapies à base de cellules NK (Natural Killer) pour 308 millions d'euros, Sanofi annonce maintenant le lancement d'un…..
Minaris Regenerative Medicine will produce Mustang Bio’s MB107 lentiviral gene therapy for the treatment of SCID
Minaris Regenerative Medicine will produce Mustang Bio's MB107 lentiviral gene therapy for the treatment of SCID Mustang Bio, a US clinical-stage biopharmaceutical company focused on cell and gene therapies for the treatment of hematologic cancers, solid tumors and rare genetic diseases, and Minaris Regenerative Medicine, a leading global contract development…..