New study expands evaluation of gene therapy for spinal muscular atrophy German researchers have just published results of a retrospective analysis of routine data collected from all patients with spinal muscular atrophy (SMA) treated with Zolgensma® (onasemnogene abeparvovec - adeno-associated viral (AAV9) vector-based gene therapy that introduces a functional copy…..
Celonic to Boost its Cell & Gene Therapy Production with Facility in the Upcoming Life Science Park Rheintal in Stein Celonic, a leading global CDMO, specialized in development and production of Advanced Therapy Medicinal Products (ATMP) and bio-therapeutics, announced a long-term lease agreement for a new production site and office…..
Trend Chart On Innovative Bioindustries - June 2020, 2nd FEATURE STORY ● Novartis snags EU nod for SMA gene therapy After a manufacturing-related delay, Novartis has won conditional approval in the EU for Zolgensma®, the one-time gene therapy to treat patients with a clinical diagnosis of SMA type 1 and…..
FEATURE STORY ● Artificial intelligence approach to create AAV capsids for gene therapies DISRUPTIVE TECHNOLOGIES ● Nanoparticles as carriers for drug delivery of macromolecules across the blood-brain barrier CLINICAL TRIALS - DATAS ● Libella gene therapeutics to run a patient paid trial of telomerase gene therapy M&A - AGREEMENTS ●…..
En 2017, le top 10 de l’industrie pharmaceutique a réalisé un chiffre d’affaires global de 322,76 milliards d’€ (+ 2,07 %) pour un bénéfice de 59,79 milliards d’€ (-14%). Ses dépenses de R&D ont atteint 64,4 milliards d’€ (+1,8%) tandis que le montant des dividendes versés aux actionnaires s’est élevé…..
Les médicaments orphelins devraient représenter 19,1 % des ventes de médicaments de prescription en 2020, soit un montant total de 176 milliards de $, selon le rapport « EvaluatePharma® Orphan Drug Report 2014 » produit par la société d’études de marché Evaluate Ltd. Avec une croissance annuelle de…..
