| Date | Product | Disease | Phase | Company | Therapeutic area |
|---|---|---|---|---|---|
| 2019-11-19 | TX200 | kidney transplantation | 1-2 | Sangamo Therapeutics (USA - CA) | Transplantation |
| 2019-07-29 | genome editing using zinc finger nucleases (ZFNs) | preclinical | Sangamo Therapeutics (USA - CA) | ||
| 2019-07-01 | allele-selective zinc finger protein transcription-factors (ZFP-TFs) | Huntington's disease | preclinical | Sangamo Therapeutics (USA - CA) | Rare diseases - Neurodegenerative diseases |
| 2019-03-28 | VY-AADC | Parkinson's disease | 1b | Voyager Therapeutics (USA-MA) | Neurological diseases - Neurodegenerative diseases |
| 2019-03-19 | zinc finger protein transcription factors (ZFP-TFs) | Tau pathology, tauopathies | preclinical | Sangamo Therapeutics (USA - CA) | Neurodegenerative diseases |
| 2019-03-08 | zinc finger nuclease (ZFN) platform technology | preclinical | Sangamo Therapeutics (USA - CA) | ||
| 2019-02-20 | ST-920 | Fabry disease | 1-2 | Sangamo Therapeutics (USA - CA) | Rare diseases - Genetic diseases |
| 2019-01-07 | dry Age-Related Macular Degeneration (AMD) | registry | Gemini Therapeutics (USA) | Ophthalmological diseases | |
| 2019-01-07 | VY-AADC | Parkinson's disease | 2 | Voyager Therapeutics (USA-MA) | Neurological diseases - Neurodegenerative diseases |
| 2018-12-17 | SB-FIX - adeno-associated virus serotype 2/6 (rAAV2/6) vectors encoding zinc finger nucleases (ZFNs) and human factor 9 gene (SB-FIX) | hemophilia B | 1-2 | Sangamo Therapeutics (USA - CA) | Rare diseases - Genetic diseases - Hematological diseases |
| 2018-10-19 | apceth-201 | acute graft-versus-host disease (aGvHD) | preclinical | apceth (Germany) | Transplantation |
| 2018-10-16 | BI-1607 (anti FcgammaRllB antibody/anti-PD1 antibody) | solid tumors | preclinical | BioInvent (Sweden) | Cancer - Oncology |
| 2018-10-16 | anti FcgammaRllB antibody/anti-PD1 antibody program | solid tumors | preclinical | BioInvent (Sweden) | Cancer - Oncology |
| 2018-10-16 | BI-1808 | solid tumors | preclinical | BioInvent (Sweden) | Cancer - Oncology |
| 2018-10-15 | BPS-804 (setrusumab) | osteogenesis imperfecta (OI) | 2b | Mereo Biopharma (UK) | Bone diseases - Metabolic diseases - Rare diseases |
| 2018-10-15 | KB103 (replication defective herpes simplex type 1 virus (HSV-1) vector expressing human COL7 protein) | dystrophic epidermolysis bullosa | 1-2 | Krystal Biotech (USA - PA) | Rare diseases - Genetic diseases - Dermatological diseases |
| 2018-10-15 | ARO-ANG3 | dyslipidemia | 1 | Arrowhead Pharmaceuticals (USA - CA) | Metabolic diseases |
| 2018-10-12 | zanubrutinib - BGB-3111 | chronic lymphocytic leukemia, small lymphocytic lymphoma, Waldenstöm's macroglobulinemia | 1 | BeiGene (China) | Cancer - Oncology |
| 2018-10-12 | evobrutinib - M2951 | relapsing multiple sclerosis (RMS) | 2 | Merck KGaA (Germany) | Autoimmune diseases - Neurodegenerative diseases |
| 2018-10-12 | Opdivo® (nivolumab) | relapsed small cell lung cancer | 3 | BMS (USA - NY) | Cancer - Oncology |