Date | Compound | Laboratory | Indication | Type of Information |
---|---|---|---|---|
2018-10-04 | transfusion-dependent beta-thalassemia (TDBT) | Orchard Therapeutics (UK) | Granting of a Fast Track status | |
2018-10-04 | transfusion-dependent beta-thalassemia (TDBT) | Orchard Therapeutics (UK) | Granting of a Fast Track status | |
2018-10-18 | influenza virus surface antigens (haemagglutinin and neuraminidase), inactivated and prepared in cell cultures, of 4 different influenza virus strains (two A subtypes and two B types) | Seqirus Netherlands, subsidiary of CSL (Australia) | prophylaxis of influenza in adults and children from 9 years of age | Positive opinion for the granting of a Market Authorisation in the EU |
2018-05-24 | replication defective herpes simplex type 1 virus (HSV-1) vector expressing human COL7 protein | Krystal Biotech (USA - PA) | dystrophic epidermolysis bullosa | Granting of a Fast Track status |
2018-08-07 | replication-incompetent, non-integrating Herpes simplex type 1 (HSV-1) vector expressing the human transglutaminase-1 (TGM-1) enzyme | Krystal Biotech (USA - PA) | TGM-1-deficient autosomal recessive congenital ichthyosis (ARCI) | Granting of the orphan status in the US |
2021-05-25 | apraglutide | VectivBio (Switzerland) | prevention of acute graft-versus-host disease | Granting of the orphan status in the US |
2021-04-01 | Lexeo Therapeutics (USA-NY) | Alzheimer's disease | Granting of a Fast Track status | |
2021-06-30 | Adeno-associated viral vector encoding the human frataxin (FXN) gene | Lexeo Therapeutics (USA-NY) | Friedreich's Ataxia | Granting of the orphan status in the US |
2021-07-12 | Adeno-associated viral vector encoding the human ceroid lipofuscinosis neuronal type 2 (CLN2) gene | Lexeo Therapeutics (USA-NY) | CLN2 Batten disease | Granting of the orphan status in the US |
2022-03-09 | Autologous ex-vivo CRISPR/Cas9 engineered Wilms¿ tumor 1-specific T-cell receptor T cells | Intellia Therapeutics (USA) | acute myeloid leukemia (AML) | Patent infringement lawsuit |
2022-05-16 | Patent infringement lawsuit |
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