Date | Compound | Laboratory | Indication | Type of Information |
---|---|---|---|---|
2016-02-01 | cell cryopreservation technology. | Reneuron (UK) | Granting of a patent | |
2016-03-16 | human coagulation factor X | Bio Products Laboratory - BPL (UK) | factor X deficiency |
Granting of a Market Authorisation in the EU |
2016-01-28 | eltrombopag | Novartis (Switzerland) | chronic idiopathic thrombocytopenic purpura (ITP) |
Positive opinion for the granting of a Market Authorisation in the EU |
2016-02-08 | synthetic peptide L-cysteine, L-cysteinylglycyl-L-glutaminyl-L-arginyl-L- .alpha.-glutamyl-L-threonyl-L-prolyl-L-.alpha.-glutamylglycyl-L-alanyl-L- .alpha.-glutamyl-L-alanyl-L-lysyl-L-prolyl-L-tryptophyl-L-tyrosyl-, cyclic (1.fwdarw.17)-disulfide | Apeptico Forschung und Entwicklung GmbH (Austria) | pseudohypoaldosteronism type 1B |
Granting of the orphan status in the US |
2015-12-14 | adeno-associated virus serotype rh10 vector encoding the human factor IX gene | Pharma Gateway (Sweden) | hemophilia B |
Granting of the orphan status in the EU |
2015-12-14 | bilayer engineered collagen hydrogel-based skin graft composed of autologous keratinocytes and fibroblasts | Voisin Consulting (France) | partial deep dermal and full thickness burns |
Granting of the orphan status in the EU |
2015-12-14 | combretastatin A1 diphosphate | Oxigene (USA - CA) Diamond Biopharm (UK) | acute myeloid leukaemia |
Granting of the orphan status in the EU |
2016-01-15 | glibenclamide | AMMTeK (France) | neonatal diabetes | Granting of the orphan status in the EU |
2015-12-14 | imetelstat | Janssen Research & Development, a J&J company (USA - NJ) | myelofibrosis |
Granting of the orphan status in the EU |
2015-12-14 | live attenuated Listeria monocytogenes bioengineered with a chimeric human epidermal growth factor receptor 2 fused to a truncated form of the Lm protein listeriolysin O | Coté Orphan Consulting UK (UK) | osteosarcoma |
Granting of the orphan status in the EU |
2016-02-17 | ex-vivo-expanded autologous fibroblasts transduced with lentiviral vector containing the COL7A1 gene | Dr Waseem Qasim (UK) | epidermolysis bullosa | Granting of the orphan status in the EU |
2016-07-27 | humanised IgG4 monoclonal antibody against total complement component 1, subcomponent s | Assign Group Development UK (UK) Bioverativ (USA - CA) | autoimmune haemolytic anaemia | Granting of the orphan status in the US |
2016-02-17 | methyl 3-((2R)-2-hydroxy-4-(((((S)-1-ethoxy-1-oxopropan-2-yl) amino)(phenoxy)phosphoryl)oxy)-3,3-dimethylbutanamido)propanoate | Retrophin (USA - NY) | pantothenate-kinase-associated neurodegeneration (PKAN) |
Granting of the orphan status in the EU |
2016-02-17 | S3,S13-cyclo(D-tyrolsyl-L-isoleucyl-L-cysteinyl-L-valyl-1-methyl-L-tryptophyl-L-glutaminyl-Laspartyl-L-tryptophyl-N-methyl-L-glycyl-L-alanyl-L-histidyl-L-arginyl-L-cysteinyl-N-methyl-Lisoleucinamide) | Amyndas Pharmaceuticals (USA - PA - Greece) | C3 glomerulopathy |
Granting of the orphan status in the EU |
2016-02-17 | 2-ethylbutyl (2S)-2-{[(S)-{[(2R,3S,4R,5R)-5-(4-aminopyrrolo[2,1-f][1,2,4]triazin-7-yl)-5-cyano-3,4-dihydroxytetrahydrofuran-2-yl]methoxy}(phenoxy)phosphoryl]amino}propanoate | Gilead Sciences (USA - CA) | Ebola fever |
Granting of the orphan status in the EU |
2016-02-17 | allogeneic fetal human retinal progenitor cells expanded ex vivo | Voisin Consulting (France) | retinitis pigmentosa |
Granting of the orphan status in the EU |
2016-02-17 | diclofenamide | Prof Michael Hanna (UK) | periodic paralysis |
Granting of the orphan status in the EU |
2016-02-17 | DNA plasmid encoding a recombinant fusion protein consisting of the extracellular domain of human TNF? p55 receptor linked to the human IgG1 Fc domain | Eyevensys (France) | non-infectious uveitis |
Granting of the orphan status in the EU |
2016-02-18 | N-(4-Methoxyphenyl)-N,2,6-trimethylfuro[2,3-d]pyrimidin-4-amine | FLAG Therapeutics (USA - NC) | glioma |
Granting of the orphan status in the US |
2016-02-17 | tolfenamic acid | RV Developpement (France) | progressive supranuclear palsy |
Granting of the orphan status in the EU |
© 2024 Biopharmanalyses - Powered by Samacom+