Date |
Product |
Disease |
Phase |
Company |
Therapeutic area |
2018-02-17
|
MOR106 |
atopic dermatitis |
1 |
Galapagos (Belgium) MorphoSys (Germany) |
Dermatological diseases |
2018-02-16
|
guselkumab (CNTO 1959) |
psoriasis |
3 |
Janssen Research & Development, a J&J company (USA - NJ) |
Autoimmune diseases - Dermatological diseases |
2018-02-15
|
Otezla® (apremilast) |
ulcerative colitis |
2 |
Celgene (USA - NJ) |
Autoimmune diseases - Inflammatory diseases - Digestive diseases |
2018-02-15
|
OPRX-106 |
ulcerative colitis |
2 |
Protalix BioTherapeutics (Israel) |
Autoimmune diseases - Inflammatory diseases - Digestive diseases |
2018-02-15
|
set of bacteriophages specifically |
inflammatory bowel disease |
1-2a |
Intralytix (USA - MA) |
Gastrointestinal diseases - Digestive diseases |
2018-02-12
|
T cells designed to express mbIL15 |
|
preclinical |
Ziopharm Oncology (USA - MA) |
Cancer - Oncology |
2018-02-12
|
Chronocort® (hydrocortisone modified release capsules) |
congenital adrenal hyperplasia (CAH) |
3 |
Diurnal Limited (UK) |
Rare diseases - Endocrine diseases - Hormonal diseases |
2018-02-12
|
AT342 |
Crigler-Najjar Syndrome |
1-2 |
Audentes Therapeutics (USA - CA) |
Rare diseases - Genetic diseases - Hepatic diseases - Liver diseases |
2018-02-09
|
tislelizumab (BGB-A317) |
advanced solid tumors - urothelial carcinoma (UC) |
1 |
BeiGene (China) |
Cancer - Oncology |
2018-02-08
|
Kevetrin® (thioureidobutyronitrile) |
ovarian cancer |
2a |
Cellceutix (USA - MA) now Innovation Pharmaceuticals (USA - MA) |
Cancer - Oncology |
2018-02-08
|
ABO-102 (SC AAV-SGSH) |
mucopolysaccharidosis type IIIA (Sanfilippo B syndrome) |
1-2 |
Abeona Therapeutics (USA - NY) |
Rare diseases - Genetic diseases |
2018-02-07
|
ABO-101 (AAV NAGLU) |
mucopolysaccharidosis type IIIB (MPS IIIB or Sanfilippo syndrome Type B) |
1-2 |
Abeona Therapeutics (USA - NY) |
Rare diseases |
2018-02-06
|
AT982 |
Pompe disease |
preclinical |
Audentes Therapeutics (USA - CA) |
Rare diseases - Genetic diseases |
2018-02-05
|
Rolontis™ (eflapegrastim) |
chemotherapy-induced neutropenia in patients with breast cancer. |
3 |
Spectrum Pharmaceuticals (USA - NV) |
Cancer - Oncology - Hematological diseases |
2018-01-31
|
tislelizumab (BGB-A317) |
advanced unresectable or metastatic esophageal squamous cell carcinoma (ESCC) |
3 |
BeiGene (China) |
Cancer - Oncology |
2018-01-24
|
Traumakine® - FP-1201 (human recombinant interferon-beta 1a) |
acute respiratory distress syndrome (ARDS) |
1 |
Faron Pharmaceuticals (Finland) |
Lung diseases - Respiratory diseases - Rare diseases |
2018-01-24
|
LN-145 |
head and neck squamous cell carcinoma (HNSCC) |
2 |
Lion Biotechnologies (USA - CA), now Iovance Biotherapeutics (USA - CA) |
Cancer - Oncology |
2018-01-18
|
nelotanserin |
Lewy Body dementia |
2 |
Axovant Sciences (USA - NY) |
Neurological diseases - CNS diseases |
2018-01-18
|
BM32 |
grass pollen allergy |
2 |
Biomay (Austria) |
Allergic diseases |
2018-01-16
|
AVXS-101 (adeno-associated virus serotype 9 expressing the human Survival Motor Neuron gene) |
spinal muscular atrophy (SMA) Type 2 |
1 |
Avexis (USA - IL) |
Rare diseases - Genetic diseases - Neuromuscular diseases |