Date |
Product |
Disease |
Phase |
Company |
Therapeutic area |
2016-07-06
|
coversin (recombinant protein derived from the saliva of the Ornithodoros moubata tick) |
paroxysmal nocturnal hemoglobinuria, atypical hemolytic uremic syndrome |
1b |
Akari Therapeutics (USA - NY - UK) |
Rare diseases |
2016-07-06
|
olipudase alfa |
acid sphingomyelinase deficiency (ASMD), also known as Niemann-Pick disease type B |
2-3 |
Sanofi Genzyme (USA - MA), a Sanofi company (France) |
Rare diseases - Genetic diseases |
2016-07-06
|
Debio 1143 - (5S,8S,10aR)-N-benzhydryl-5-((S)-2-(methylamino)propanamido)-3-(3-methylbutanoyl)-6-oxodecahydropyrrolo[1,2-a][1,5]diazocine-8-carboxamide |
epithelial ovarian cancer |
2 |
Debiopharm (Switzerland) |
Cancer - Oncology |
2016-07-05
|
napabucasin (BBI608) |
non squamous non cell lung cancer |
3 |
Boston Biomedical (USA - MA) |
Cancer - Oncology |
2016-07-03
|
GS010- adeno-associated viral vector containing the human NADH dehydrogenase 4 gene |
Leber hereditary optic neuropathy (LHON) |
1-2 |
Gensight Biologics (France) |
Ophtalmological diseases - Genetic diseases - Rare diseases |
2016-07-01
|
ONCOS - 102 |
malignant pleural mesothelioma |
1-2 |
Targovax (Norway) |
Cancer - Oncology |
2016-07-01
|
ANYARA (naptumomab estafenatox) |
renal cell cancer |
2-3 |
Active Biotech (Sweden) |
Cancer - Oncology |
2016-06-30
|
AGS62P1 |
acute myeloid leukemia |
1 |
Astellas Pharma (Japan) Agensys (USA - CA) |
Cancer - Oncology |
2016-06-30
|
QGC001 |
chronic heart failure |
2a |
Quantum Genomics (France) |
Cardiovascular diseases |
2016-06-30
|
Ofev® (nintedanib) |
idiopathic pulmonary fibrosis (IPF) |
3 |
Boehringer Ingelheim (Germany) |
Lung diseases - Respiratory diseases - Rare diseases |
2016-06-30
|
SHP607 |
retinopathy of prematurity |
2 |
Shire (UK - USA) |
Rare diseases |
2016-06-29
|
Rydapt®(midostaurin - PKC412) |
advanced systemic mastocytosis |
2 |
Novartis (Switzerland) |
Rare diseases |
2016-06-29
|
GBT440 |
sickle cell disease |
2a |
Global Blood Therapeutics (USA - CA) |
Rare diseases - Genetic diseases - Hematological diseases |
2016-06-28
|
ND0612H |
Parkinson's disease |
1 |
Neuroderm (Israel) |
Neurodegenerative diseases |
2016-06-28
|
XOMA 213 |
prolactinomas |
2 |
Xoma (USA - CA) |
Endocrinological diseases - Hormonal diseases |
2016-06-28
|
pembrolizumab (MK-3475) |
triple negative breast cancer (TNBC) |
3 |
Merck&Co (USA - NJ) |
Cancer - Oncology |
2016-06-27
|
patiromer |
hyperkalemia |
3 |
Relypsa (USA - CA) |
Cardiovascular diseases - Metabolic diseases |
2016-06-27
|
Epidiolex® (cannabidiol (2-[(1R,6R)-3-Methyl-6-(1-methylethenyl)-2-cyclohexen-1-yl]-5-pentyl-1,3-benzenediol) |
Lennox-Gastaut syndrome |
3 |
Shire (UK - USA) |
Rare diseases - CNS diseases - Neurological diseases |
2016-06-22
|
Zika virus diagnostics |
Zika virus infection |
|
Avacta (UK) |
Infectious diseases |
2016-06-21
|
Halaven® (eribulin) |
unresectable locally advanced liposarcoma and leiomyosarcoma |
3 |
Eisai (Japan) |
Cancer - Oncology |