Date |
Product |
Disease |
Phase |
Company |
Therapeutic area |
2017-03-09
|
BGB-3111 |
relapsed or refractory chronic lymphocytic leukemia (CLL) or small lymphocytic lymphoma (SLL) |
2 |
BeiGene (China) |
Cancer - Oncology |
2017-03-06
|
volanesorsen (ISIS-APOCIII Rx) |
familial chylomicronemia syndrome |
3 |
Ionis Pharmaceuticals (USA - CA) Akcea Therapeutics (USA - MA) |
Rare diseases - Genetic diseases - Metabolic diseases |
2017-03-06
|
SD-101 and Keytruda® (pembrolizumab) |
metastatic melanoma |
1b-2 |
Dynavax (USA - CA) |
Cancer - Oncology |
2017-03-06
|
M1095 |
psoriasis |
1b |
Merck KGaA (Germany) |
Autoimmune diseases - Dermatological diseases |
2017-03-06
|
SGN-CD33A (vadastuximab talirine) |
relapsed or refractory acute myeloid leukemia (AML) |
1-2 |
Seattle Genetics (USA - WA) |
Cancer - Oncology |
2017-03-04
|
Taltz® (ixekizumab) |
plaque psoriasis |
3 |
Eli Lilly (USA - IN) |
Autoimmune diseases - Dermatological diseases |
2017-03-03
|
TG4010 and Opdivo® (nivolumab) |
metastatic non-small-cell lung cancer (NSCLC) |
2 |
University of California, Davis, (USA - CA) Transgene (France) BMS (USA - NY) |
Cancer - Oncology |
2017-03-03
|
guselkumab (CNTO 1959) |
psoriasis |
3 |
Janssen Research & Development, a J&J company (USA - NJ) |
Autoimmune diseases - Dermatological diseases |
2017-03-02
|
Alprolix® (eftrenonacog alfa - long-lasting recombinant Factor IX Fc fusion protein (rFIXFc) - BIIB 029 |
hemophilia B |
3 |
Bioverativ (USA - MA) Swedish Orphan Biovitrum SOBI (Sweden) |
Hematologic diseases - Genetic diseases - Rare diseases |
2017-03-02
|
BGB-3111 |
relapsed or refractory mantle cell lymphoma |
2 |
BeiGene (China) |
Cancer - Oncology |
2017-03-02
|
Translarna™ (ataluren) |
nonsense mutation cystic fibrosis (nmCF) |
3 |
PTC Therapeutics (USA - NJ) |
Rare diseases - Genetic diseases |
2017-03-02
|
CHS-1420 (biosimilar version of Humira® (adalimumab)) |
|
|
Coherus Biosciences (USA - CA) |
|
2017-03-01
|
voclosporin |
lupus nephritis |
2b |
Aurinia Pharmaceuticals (Canada) |
Autoimmune diseases – Inflammatory diseases - Renal diseases |
2017-03-01
|
|
Crigler-Najjar Syndrome |
|
Audentes Therapeutics (USA - CA) |
Hepatic diseases - Liver diseases |
2017-03-01
|
STR001 (pioglitazone) |
hearing loss, preservation of residual hearing in patients undergoing cochlear implantation surgery |
preclinical |
Strekin (Switzerland) |
Otorhinolaryngology |
2017-03-01
|
STR001 (pioglitazone) |
preservation of residual hearing in patients undergoing cochlear implantation surgery |
2 |
Strekin (Switzerland) |
Otorhinolaryngology |
2017-02-28
|
radezolid |
mild-to-moderate acne |
1 |
Melinta Therapeutics (USA - CT) |
Dermatological diseases |
2017-02-28
|
|
C3 glomerulopathy |
natural history |
Achillion Pharmaceuticals (USA - CT) Imperial College London (UK) |
Rare diseases - Renal diseases - Kidney diseases |
2017-02-28
|
resminostat (oral pan-histone deacetylase (HDAC) inhibitor) |
advanced-stage cutaneous T-cell lymphoma (CTCL) |
preclinical |
4SC (Germany) |
Cancer - Oncology |
2017-02-27
|
ORY-2001 |
multiple sclerosis |
preclinical |
Oryzon Genomics (Spain) |
Neurodegenerative diseases |